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What a $2 Million Per Dose Gene Therapy Reveals About Drug Pricing

ProPublica • Published on 11 Feb 2025 • ~5850 words
Robin Fields reports on Zolgensma, a groundbreaking gene therapy priced at over $2 million per dose. The drug’s early development was funded by taxpayers and small charities, but in the end, executives, VCs, and Novartis reaped the profits.
The story of Zolgensma lays bare a confounding reality about modern drug development, in which revolutionary new treatments are becoming available only to be priced out of reach for many. It’s a story that upends commonly held conceptions that high drug prices reflect huge industry investments in innovation. Most of all, it’s a story that prompts, again and again, an increasingly urgent question: Do medical advances really have to be this expensive?
Wall Street analysts predicted Novartis’ new prize drug would be the first therapy to smash the million-dollar-a-dose mark. The Swiss colossus crafted a sophisticated campaign to justify more than double that amount, enlisting a team of respected academics, data-modelers and pricing strategists to help make its case.

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Added on 13 Feb 2025 09:11

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